Boy With Rare Brain Disease Treated at GH

Photograph of the two boys with GH insensitivity at ages 4 and 2.5

Inspiring North Carolina girl, 8, has terminal childhood DEMENTIA

Family awarded $30 million after baby delivered at MGH suffers

Boy With Rare Brain Disease Treated at GH

Surviving rare childhood brain cancer

Tay Sachs Disease - Symptoms, Causes, Treatment

Opinion: I want to cure my son of his rare genetic disease. Is

Oxford company working on drug to treat rare brain disease - BBC News

Comprehensive study of 28 individuals with SIN3A-related disorder

Facial appearance of one-year-old girl with WiedemannSteiner

This 1-year-old just met the only doctor who may be able to cure